Sfoglia per Autore
Mostrati risultati da 1 a 5 di 5
The role of ABC transporters in protecting cells from bilirubin toxicity
2009-01-01 Bellarosa, Cristina; Bortolussi, Giulia; Tiribelli, Claudio
Rescue of bilirubin-induced neonatal lethality in a mouse model of Crigler-Najjar syndrome type I by AAV9-mediated gene transfer.
2012-01-01 Bortolussi, Giulia; Zentilin, Lorena; Baj, Gabriele; Giraudi, PABLO JOSÈ; Bellarosa, Cristina; Giacca, Mauro; Tiribelli, Claudio; Muro, A. F.
Life-long correction of hyperbilirubinemia with a neonatal liver-specific AAV-mediated gene transfer in a lethal mouse model of Crigler-Najjar Syndrome.
2014-01-01 Bortolussi, Giulia; Zentillin, L; Vaníkova, J; Bockor, L; Bellarosa, Cristina; Mancarella, Antonio; Vianello, Eleonora; Tiribelli, Claudio; Giacca, Mauro; Vitek, L; Muro, A. f.
Coupling AAV-mediated promoterless gene targeting to SaCas9 nuclease to efficiently correct liver metabolic diseases
2019-01-01 De Caneva, A.; Porro, F.; Bortolussi, G.; Sola, R.; Lisjak, M.; Barzel, A.; Giacca, M.; Kay, M. A.; Vlahovicek, K.; Zentilin, L.; Muro, A. F.
Fludarabine increases nuclease-free AAV- and CRISPR/Cas9-mediated homologous recombination in mice
2022-01-01 Tsuji, Shinnosuke; Stephens, Calvin J; Bortolussi, Giulia; Zhang, Feijie; Baj, Gabriele; Jang, Hagoon; de Alencastro, Gustavo; Muro, Andrés F; Pekrun, Katja; Kay, Mark A
Mostrati risultati da 1 a 5 di 5
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